Tag: Gene Therapy

New perspective on the role of sRNAs in the diseaseCredit: UNIVERSITY OF BARCELONA Huntington's disease is caused by a mutation ...

CRISPR gene editing has transformed research, but it is not perfect, and can sometimes target unintended genes; to watch CRISPR ...

Inhibiting a gene involved in the abnormal growth of blood vessels in certain ocular disorders may reduce retinal neovascularization, researchers ...

Machine learning study initiated at the Wyss Institute in collaboration with Google Research enables unprecedented AAV capsid diversification with potential ...

Division of synthetic gene circuit workloads will make therapy more effective.Credit: Graphic created by Xiaojun Tian/ASU. A new process for ...

Credit: Composite photo by L. Brian Stauffer CHAMPAIGN, Ill. -- Researchers used single-molecule imaging to compare the genome-editing tools CRISPR-Cas9 ...

Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, January 26, 2021--Hybrid closed-loop insulin therapy improved glycemic control in adolescents ...

Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, January 19, 2021--Gene editing therapies, including CRISPR-Cas systems, offer the potential ...

Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, January 15, 2021--The biodistribution of adeno-associated virus (AAV) gene transfer vectors ...

Distant genes can be neighborsCredit: UIC Genome analysis can provide information on genes and their location on a strand of ...

Study demonstrates the efficacy and therapeutic potential of select ionizable lipid nanoparticles for delivering mRNA to treat genetic diseases before ...

The study was carried out with data from 89 patients admitted to the IFEMA HospitalCredit: CNIO Patients with severe COVID-19 ...

Using a recently developed DNA base-editing technique, researchers correct accelerating aging disorderCredit: Ernesto del Aguila III, NHGRI Researchers have successfully ...

Why aggressive subtype can resist treatmentCredit: The Hospital Research Foundation Australian research has identified a new mechanism in which prostate ...

Brain tumours might arise when tissue does not heal properly-- a finding that opens up new ideas about how cancer ...

Breakthrough may help in the treatment of children with hearing lossCredit: Tel Aviv University A new study from Tel Aviv ...

Credit: Salk Institute LA JOLLA--(December 22, 2020) Assistant Professor Dmitry Lyumkis has received a Faculty Early Career Development Program (CAREER) ...

They have used precision medicine to uncover and treat new skeletal disordersCredit: University of Malaga Researchers of the "Cell Biology ...

Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, December 15, 2020--A new study identified an adenovirus gene therapy vector ...

Credit: Courtesy Civelek lab Researchers at the University of Virginia have shed light on how our genes affect our risk ...