New therapeutic target for Huntington’s treatment
New perspective on the role of sRNAs in the diseaseCredit: UNIVERSITY OF BARCELONA Huntington's disease is caused by a mutation ...
Tag: Gene Therapy
Scientists use DNA origami to monitor CRISPR gene targeting
CRISPR gene editing has transformed research, but it is not perfect, and can sometimes target unintended genes; to watch CRISPR ...
New therapeutic approach may help treat age-related macular degeneration effectively
Inhibiting a gene involved in the abnormal growth of blood vessels in certain ocular disorders may reduce retinal neovascularization, researchers ...
Machine-learning how to create better AAV gene delivery vehicles
Machine learning study initiated at the Wyss Institute in collaboration with Google Research enables unprecedented AAV capsid diversification with potential ...
Winner-takes-all synthetic gene circuit process opens new pathways to disease treatment
Division of synthetic gene circuit workloads will make therapy more effective.Credit: Graphic created by Xiaojun Tian/ASU. A new process for ...
Genome-editing tool TALEN outperforms CRISPR-Cas9 in tightly packed DNA
Credit: Composite photo by L. Brian Stauffer CHAMPAIGN, Ill. -- Researchers used single-molecule imaging to compare the genome-editing tools CRISPR-Cas9 ...
Hybrid closed-loop insulin therapy improves glycemic control
Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, January 26, 2021--Hybrid closed-loop insulin therapy improved glycemic control in adolescents ...
Genome editing to treat human retinal degeneration
Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, January 19, 2021--Gene editing therapies, including CRISPR-Cas systems, offer the potential ...
Biodistribution of AAV gene transfer vectors in nonhuman primate
Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, January 15, 2021--The biodistribution of adeno-associated virus (AAV) gene transfer vectors ...
Reverse engineering 3D chromosome models for individual cells
Distant genes can be neighborsCredit: UIC Genome analysis can provide information on genes and their location on a strand of ...
Researchers identify nanoparticles that could deliver therapeutic mRNA before birth
Study demonstrates the efficacy and therapeutic potential of select ionizable lipid nanoparticles for delivering mRNA to treat genetic diseases before ...
A CNIO study links severe COVID-19 disease to short telomeres
The study was carried out with data from 89 patients admitted to the IFEMA HospitalCredit: CNIO Patients with severe COVID-19 ...
DNA-editing method shows promise to treat mouse model of progeria
Using a recently developed DNA base-editing technique, researchers correct accelerating aging disorderCredit: Ernesto del Aguila III, NHGRI Researchers have successfully ...
New clues to prostate cancer
Why aggressive subtype can resist treatmentCredit: The Hospital Research Foundation Australian research has identified a new mechanism in which prostate ...
Brain cancer linked to tissue healing
Brain tumours might arise when tissue does not heal properly-- a finding that opens up new ideas about how cancer ...
Scientists at Tel Aviv University develop new gene therapy for deafness
Breakthrough may help in the treatment of children with hearing lossCredit: Tel Aviv University A new study from Tel Aviv ...
Salk Assistant Professor Dmitry Lyumkis receives CAREER award from NSF
Credit: Salk Institute LA JOLLA--(December 22, 2020) Assistant Professor Dmitry Lyumkis has received a Faculty Early Career Development Program (CAREER) ...
Researchers identify a rare genetic bone disorder through massive sequencing methods
They have used precision medicine to uncover and treat new skeletal disordersCredit: University of Malaga Researchers of the "Cell Biology ...
Gene therapy for placental insufficiency moves toward the clinic
Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, December 15, 2020--A new study identified an adenovirus gene therapy vector ...
Gene discovery could help prevent heart attacks
Credit: Courtesy Civelek lab Researchers at the University of Virginia have shed light on how our genes affect our risk ...
