What can be done to prevent another CRISPR crisis?
The public announcement last fall from China regarding gene editing on human embryos, conducted without the benefit of scientific review ...
Tag: Gene Therapy
Researcher gets $3.3 million grant to develop universal treatment for cystic fibrosis
CORVALLIS, Ore. - A pharmaceutical sciences researcher at Oregon State University has received a five-year, $3.3 million grant from the ...
Gene repair improves memory and seizures in adult autism model
Credit: Scott Wiseman for Scripps Research JUPITER, Fla. - April 29, 2019 - A new study challenges the presumption that ...
Hypersociability in Williams syndrome result of Myelination deficits
Axon 'insulating tape' suffers from gene deletion that causes social impairment associated with rare disorder, Tel Aviv University researchers say ...
Personalizing precision medicine with combination therapies improves outcomes in cancer
Precision oncology often relies on treating patients with a single, molecularly matched therapy that targets one mutation in their tumor. ...
New method to detect off-target effects of CRISPR
Scientists discover how to identify off-target damage caused by CRISPR genome editing SAN FRANCISCO, CA--April 19, 2019--Since the CRISPR genome ...
Estimating the efficacy and cost of curative gene therapy for beta-thalassemia
Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, April 18, 2019--Gene therapy offers the promise of a cure for ...
A light-activated remote control for cells
What if doctors had a remote control that they could use to steer a patient's own cells to a wound ...
New study first to identify cause of rare genetic metabolic disorder
A new study from BC Children's Hospital, the University of British Columbia (UBC) and an international team of researchers published ...
Engineering ‘hairpins’ increases CRISPR accuracy
Added piece of RNA could improve the precision of CRISPR 50-foldCredit: Les Todd DURHAM, N.C. -- Biomedical engineers at Duke ...
Scanning for cancer treatment
Researchers combine CRISPR gene-editing technology with drug discovery to understand why treatment works (or doesn't)Credit: The Armed Forces Institute of ...
Cancer-killing combination therapies unveiled with new drug-screening tool
Method IDs which targeted therapies, inadequate on their own, can be paired up to kill non-responsive cancers UC San Francisco ...
UConn and Foundation for Prader Willi Research create stem cell biobank
A centralized, high-quality bank of stem cells will help researchers better understand Prader Willi SyndromeCredit: Yaling Liu/UConn A new collaboration ...
A new DFG Research Unit for rare genetic diseases
How can we improve the identification and prompt diagnosis of genetic diseases? A new Research Unit at Charité - Universitätsmedizin ...
Opitz C Syndrome: New advances to improve the genetic diagnose of an ultra-rare disease
When the early diagnose is mistakenCredit: UNIVERSITY OF BARCELONA Opitz C syndrome (OCS), an ultra-rare disease that causes serious physical ...
Russian Science Foundation grant winners for 2019 announced
19 winning bids are from Kazan University Every project is to receive from 4 to 6 million rubles during the ...
Natural gene therapy for intractable skin disease discovered
Credit: Suzuki S. et al., Life Science Alliance, February 4, 2019 Pathogenic gene mutations causing a type of intractable skin ...
Introducing a kinder, gentler way to blow holes in cells
For injecting CRISPR-Cas9 into cells, new technique is more efficient, simpler and cheaperCredit: Yuhong Cao, UC Berkeley When scientists attempt ...
Researchers at Dana-Farber/Boston Children’s optimize gene editing for SCD and beta thalassemia
New strategy for editing blood stem cells is more efficient and targetedCredit: Daniel Bauer/Boston Children's Hospital Researchers at Dana-Farber/Boston Children's ...
New study confirms EpCAM as promising target for cancer immunotherapy
Credit: Mary Ann Liebert Inc., publishers New Rochelle, NY, March 28, 2019--Researchers have shown that cancer immunotherapy targeting the tumor ...
