New gene therapy research at Neuroscience 2019
Live-streamed press conference offers breaking researchCredit: Society for Neuroscience Gene therapy shows promise as a way to treat and cure ...
Tag: Gene Therapy
New CRISPR class expands genetic engineering toolbox
The new approach opens up nearly 90 percent of CRISPR-Cas systems for use in human cells, including biomedical research and ...
World’s first gene therapy for glycogen storage disease produces remarkable results
Consuming cornstarch every few hours has been the only available option for survivalCredit: Tina Encarnacion/UConn Health At the Association for ...
Gene editing enables researchers to correct mutation in muscle stem cells in DMD model
Correction of mutation in muscle stem cells with CRISPR editing may pave the way for lifelong treatments for muscular dystrophyCredit: ...
Gene-targeted cancer drugs, slow release overcome resistance
Promising cancer therapy overcomes body's innate resistance using CRISPR/Cas targeting and drug delivery gelCredit: Mandana Manzari DURHAM, N.C.-- Biomedical engineers ...
Children’s Tumor Foundation hosts NF Innovation Week in San Francisco
Researchers, clinicians, data scientists, patients and caregivers convene to fast-track cures for the rare disorder neurofibromatosis Neurofibromatosis (NF), a genetic ...
Tiny bubbles in our body could fight cancer better than chemo
EAST LANSING, Mich. - Healthy cells in our body release nano-sized bubbles that transfer genetic material such as DNA and ...
ASHG honors Huda Zoghbi with Victor A. McKusick Leadership Award
Neurologist to Receive Award at ASHG 2019 Annual MeetingCredit: courtesy Dr. Zoghbi ROCKVILLE, MD - The American Society of Human ...
ASHG to launch Human Genetics and Genomics Advances, a new open access journal
ASHG's flagship publication The American Journal of Human Genetics reaffirms commitment to reflect full breadth and reach of field ROCKVILLE, ...
New insight into microRNA function can give gene therapy a boost
Scientists at the University of Eastern Finland and the University of Oxford have shown that small RNA molecules occurring naturally ...
OSU researcher expands research into deadly muscle-wasting syndrome
CORVALLIS, Ore. - An Oregon State University scientist has received a $2.3 million, five-year grant to build on his promising ...
Novel nanoparticles deliver CRISPR gene editing tools into the cell with much higher efficiency
Researchers used lipid nanoparticles to deliver CRISPR/Cas9 gene editing tools for potential treatment of hyperlipidemia.Credit: From animation by Visual Science ...
Clinical trial for new anti-obesity drug ready to launch at University of Alberta
University of Alberta clinical researcher leading genetic study with drug trial to help patients with rare genetic disorders lose weight.Credit: ...
Keeping do-it-yourself gene science safe
CWRU team will provide policy recommendations for balancing safety, innovationCredit: Case Western Reserve University School of Law While federal and ...