A new DFG Research Unit for rare genetic diseases
How can we improve the identification and prompt diagnosis of genetic diseases? A new Research Unit at Charité - Universitätsmedizin ...
Tag: Gene Therapy
Opitz C Syndrome: New advances to improve the genetic diagnose of an ultra-rare disease
When the early diagnose is mistakenCredit: UNIVERSITY OF BARCELONA Opitz C syndrome (OCS), an ultra-rare disease that causes serious physical ...
Russian Science Foundation grant winners for 2019 announced
19 winning bids are from Kazan University Every project is to receive from 4 to 6 million rubles during the ...
Natural gene therapy for intractable skin disease discovered
Credit: Suzuki S. et al., Life Science Alliance, February 4, 2019 Pathogenic gene mutations causing a type of intractable skin ...
Introducing a kinder, gentler way to blow holes in cells
For injecting CRISPR-Cas9 into cells, new technique is more efficient, simpler and cheaperCredit: Yuhong Cao, UC Berkeley When scientists attempt ...
Researchers at Dana-Farber/Boston Children’s optimize gene editing for SCD and beta thalassemia
New strategy for editing blood stem cells is more efficient and targetedCredit: Daniel Bauer/Boston Children's Hospital Researchers at Dana-Farber/Boston Children's ...
New study confirms EpCAM as promising target for cancer immunotherapy
Credit: Mary Ann Liebert Inc., publishers New Rochelle, NY, March 28, 2019--Researchers have shown that cancer immunotherapy targeting the tumor ...
Interest in RNA editing heats up
The gene-editing technology known as CRISPR has attracted much excitement and investor interest with its potential to someday treat diseases ...
Researchers optimize aptamer with enhanced myelin-binding properties for MS treatment
Credit: Mary Ann Liebert, Inc., publishers New Rochelle, NY, March 27, 2019--A new study has demonstrated the enhanced ability of ...
Rejuvenation of aging cells helps to cure osteoarthritis through gene therapy
Credit: IOZ Aging is a risk factor for the development of osteoarthritis (OA), a chronic disease characterized by degeneration of ...
Researchers reveal new molecular mechanism involved in pancreas repair
Researchers at the University of Malaga (UMA) demonstrate that Wt1 gene deletion causes deterioration of this organCredit: University of Malaga ...
City of Hope scientists showcase new findings at the 2019 AACR meeting
Researchers will discuss data and ongoing studies involving CAR T cell therapy, advanced nonsmall cell lung cancer, use of natural ...
Gene medication to help treat spinal cord injuries
The new research aims to regenerate nervous tissue The two-gene medication has been proven to recover motor functions in rats. ...
With single gene insertion, blind mice regain sight
Opsins make 'blind' cells light-sensitive; potential human treatment within three yearsCredit: John Flannery, UC Berkeley It was surprisingly simple. University ...
Researchers find epigenetic loss that changes how cells obtain energy from cancer
Cheap energy for the tumor cellCredit: UNIVERSITY OF BARCELONA It has been known for decades that cancer cells have an ...
BPS and Rep. Bill Foster host Dr. Jennifer Doudna for CRISPR-101 Briefing
Sean Winkler - BPS; Rep. Foster; Dr. Jennifer Doudna; Jennifer Pesanelli - BPS view more Washington, DC - On March ...
Therapy could improve and prolong sight in those suffering vision loss
Damping noise in hyperactive eye cells allows details to emerge Millions of Americans are progressively losing their sight as cells ...
International congress of Myology 2019
At Bordeaux (France) from March 25 to 28, 2019 During the 3 days of plenary sessions and thematic symposia of ...
Guidelines on the use of genetic testing in psychiatry
International Society Issues StatementCredit: ISPG An expert committee of psychiatrists and geneticists has issued revised guidelines for the use of ...
New diagnostic clues found for life limiting lung condition
A new biomarker that could be used to provide earlier diagnosis for a life limiting lung condition has been identified ...
