New gene editor harnesses jumping genes for precise DNA integration
Credit: Sam Sternberg/Columbia University Irving Medical Center NEW YORK, NY --A new discovery by researchers at Columbia University Vagelos College ...
Tag: Gene Therapy
New tool can pinpoint origins of the gut’s bacteria
Credit: UCLA Samueli Engineering A UCLA-led research team has developed a faster and more accurate way to determine where the ...
Groundbreaking DNA study launched to discover new connections between genetics & diseases
Study represents largest DNA mapping effort undertaken in US from a single populationCredit: Intermountain Healthcare REYKJAVIK, ICELAND, and SALT LAKE ...
Drug to treat malaria could mitigate hereditary hearing loss
Drug activates sensory proteins in aquatic model of human hearingCredit: CWRUSOM & PNAS The ability to hear depends on proteins ...
Scientists edge closer to root causes of multiple sclerosis
Credit: University of British Columbia An international team of researchers led by the University of British Columbia has made a ...
NIH funds clinical trials using genomics to treat chronic diseases
A new phase of the IGNITE Network will conduct clinical trials of genomic medicine interventionsCredit: Ernesto Del Aguila III, NHGRI ...
Brighter possibilities for treating blindness
Review published in the 10th anniversary series of science Translational Medicine Advances in preclinical research are now being translated into ...
Germline gene therapy pioneer, teenage son make case for safe treatment
OHSU's Shoukhrat Mitalipov, son publish perspective in Nature MedicineCredit: OHSU/Kristyna Wentz-Graff An internationally known embryologist and his son make the ...
New genetic weapons challenge sickle cell disease
Rice University lab's CRISPR-Cas9 strategy offers two-pronged attackCredit: Jeff Fitlow/Rice University HOUSTON - (June 3, 2019) - Help for patients ...
From viruses to social bots, researchers unearth the structure of attacked networks
A new statistical machine learning framework gleans the invisible and unobservable structure of any attacked network The human body's mechanisms ...
Genethon emphasizes its decisive role in the first gene therapy for a neuromuscular diseas
On May 24, the Food and Drug Administration approved Zolgensma®, a gene therapy drug for the treatment of spinal muscular ...
Could gold be the key to making gene therapy for HIV, blood disorders more accessible?
A proof-of-principle study published in Nature Materials shows that gold nanoparticles loaded with CRISPR and other gene-editing tools safely and ...
Gene therapy towards a clinical trial for gamma-sarcoglycanopathy, limb-girdle muscular dystrophy
Gamma-sarcoglycanopathy (LGMD2C) is one of the most common limb-girdle myopathies. It affects less than 10 people per 1,000,000 and is ...
CNIO participates in a study identifying a novel oncogene for most common types of blood cancer
Miguel Gallardo, researcher and coordinator of the H12O-CNIO Haematological Malignancies Clinical Research Unit headed by Joaquín Martínez at the Spanish ...