Shirguppe, S., Gapinske, M., Swami, D. et al. In vivo CRISPR base editing for treatment of Huntington’s disease.
Nat. Biomed. Eng (2026). https://doi.org/10.1038/s41551-026-01747-y
https://doi.org/10.1038/s41551-026-01747-y
Tags: advancements in neurogenetic therapiesbiomedical engineering in neurogeneticsCRISPR technology in Huntington’s diseaseCRISPR-based gene correction in vivogene editing in neurodegenerative disordersgenome editing for hereditary neurological disordersHuntington’s disease genetic mutation targetingin vivo CRISPR base editing for Huntington’s disease treatmentin vivo gene therapy strategiesmolecular mechanisms of Huntington’s diseasetargeted genetic therapy for Huntington’stherapeutic potential of CRISPR in neurodegeneration
